Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.

A protein called MYOD has long been known to be able to turn on genes, but a recent study has found that it also can turn off ...

Columnist Shalom Lin and his partner, Amanda — both disabled artists — find that their challenges are exactly what can drive ...

Enrollment is now ongoing in a first-in-human clinical trial testing EPI-321, a therapy designed to target the underlying ...

The FDA has granted breakthrough therapy designation to DYNE-251 for the treatment of DMD in patients amenable to exon 51 ...

In both good times and bad, the importance of human connection cannot be understated, columnist Patrick Moeschen writes.

View this post on Instagram Day 2 of 30 Days of MD Topic: Being a Teenager This is Kimberly Mullis’ story: Hey fam, I’m Kimmy!! (The one in the middle:) I have SMA II, and am truly living my best ...

View this post on Instagram Day 8 of 30 Days of MD Topic: Poem About MD This is @writingpoemsinthedark’s story: Simply put, I write to connect. Poetry allows me to address and work through topics that ...

View this post on Instagram Day 8 of #30daysofMD - Casey Duffield’s Story Accommodations and MD I think the word accommodation needs some accommodating. As someone who looks relatively healthy and ...

View this post on Instagram Day 28 of 30 Days of MD Topic: Genetics and Gardening This is @cocohollywood’s story: Lurking in my mom’s genetics is FSH muscular dystrophy (facioscapulohumeral muscular ...

All of those with FSHD are on unique paths, writes columnist Robin Stemple, but feedback from fellow patients is still immensely valuable.