Multidisciplinary coordination across prescribing teams, nursing, laboratory medicine, finance, and infusion centers is crucial for gene therapy delivery in Duchenne muscular dystrophy (DMD).

A Monell Chemical Senses Center study published this week in the Journal of Clinical Investigation offers renewed hope for ...

Just a few weeks after closing a $155 million series B, RNA editing biotech AIRNA is bringing an experienced gene therapy ...

The researchers analyzed gene and protein expression, along with lipid profiles, in the bone marrow of mice whose Elovl2 gene ...

The prospects for a one-time treatment that reduces the risk of heart disease for the rest of a person’s life just got ...

Getting therapeutic drugs past the blood-brain barrier has long been a major challenge in treating brain diseases. Now, researchers have explored how cholesterol-modified heteroduplex oligonucleotides ...

Sarepta Therapeutics SRPT announced updates from its clinical programs, which focus on targeting different subtypes of limb-girdle muscular dystrophy (LGMD), a group of rare genetic disorders marked ...

But IV nutrition therapy has also become popular among the wellness crowd in recent years, thanks to potential perks such as fighting fatigue, boosting immunity, and easing stress. IV nutrition ...