Echocardiography may be at the vanguard for early and rapid detection of heart issues indicative of Duchenne muscular ...

The city of Rockford dedicated a memorial plaque to one of their own, who died in November to a form of muscular dystrophy.

This September, the Muscular Dystrophy Association (MDA) is launching its milestone #MDAstrong campaign during a historic moment for the organization: its 75th anniversary. The campaign reframes what ...

The FDA’s shift on Elevidys sends a message: boldness, scientific rigor and urgency are essential in confronting rare ...

Sarepta Therapeutics has provided additional safety data on its gene therapy Elevidys as a Duchenne muscular dystrophy ...

Managing osteoporosis and bone health in Duchenne muscular dystrophy occurs in a high-risk environment for fractures due to disease-related loss of muscle and movement, adverse effects of ...

After deaths and FDA setbacks, Sarepta abandoned LGMD gene therapy, leaving families desperate and patients without ...

Sarepta Therapeutics’ Duchenne muscular dystrophy gene therapy fell short of its main Phase 3 goal, but the firm contends the full body of evidence supports expanding the therapy’s label to ...

Duchenne muscular dystrophy, a rare genetic disorder with which some 300-600 boys are born each year, is characterized by progressive muscle weakness and loss. Using a mouse model of the disease ...