Muscular Dystrophy News2h
What success looks like for me as a DMD parent
As a parent and caregiver to three sons with DMD, columnist Betty Vertin's definition of what success looks like has changed over the years.
Muscular Dystrophy News1d
FDA awards fast track designation to DM1 treatment DYNE-101
The FDA has granted fast track designation to DYNE-101, a therapy for myotonic dystrophy type 1 (DM1) now in testing in a ...
Muscular Dystrophy News2d
Corticosteroid at low dose may help with muscle damage, inflammation
A pilot study in 19 LGMD patients and one with Becker MD found low-dose prednisone helped lower markers of muscle damage and ...
Muscular Dystrophy News7d
Stuck in limbo with both accessible vans out of commission
I live in rural Nebraska with my husband and our seven children. Three of them — Max, 19; Rowen, 15; and Charlie, 14 — live with Duchenne muscular dystrophy (DMD). People who meet me in person for the ...
Muscular Dystrophy News8d
DYNE-101 is leading to functional gains for DM1 patients in trial
The investigational therapy DYNE-101 worked as expected and led to functional improvements for people with myotonic dystrophy type 1 (DM1) in a clinical trial, according to an update from developer ...